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Gene therapy for hemophilia B mice with scAAV8-LP1-hFIX 期刊论文
FRONTIERS OF MEDICINE, 2016, 卷号: 10, 期号: 2
作者:  Lu, Wei;  Zhou, Qingzhang;  Yang, Hao;  Wang, Hao;  Gu, Yexing
收藏  |  浏览/下载:3/0  |  提交时间:2019/12/06
Gene Therapy for Hemophilia B With Liver-specific Element Mediated by Rep-RBE Site-specific Integration System 期刊论文
JOURNAL OF CARDIOVASCULAR PHARMACOLOGY, 2015, 卷号: 65, 期号: 2
作者:  Xu, Zhengxin;  Ye, Juan;  Zhang, Amin;  Xie, Linjun;  Shen, Qi
收藏  |  浏览/下载:10/0  |  提交时间:2019/12/13
hFIX双筛选定点整合系统的研究及两个整合相关蛋白的初步探索 学位论文
2014
作者:  阮婕
收藏  |  浏览/下载:2/0  |  提交时间:2019/12/19
A 16-bp RBE element mediated Rep-dependent site-specific integration in AAVS1 transgenic mice for expression of hFIX 期刊论文
GENE THERAPY, 2009, 卷号: 16, 期号: 5
作者:  Xu, Z. X.;  Chen, J. Z.;  Yue, Y. B.;  Zhang, J. Q.;  Li, Z. H.
收藏  |  浏览/下载:8/0  |  提交时间:2019/12/19
The RBE Mediation Rep-Dependent Site-Specific Integration and hFIX Expression in Transgene Mice 会议论文
作者:  Chen, Jin-Zhong;  Xue, Jing-Lun
收藏  |  浏览/下载:1/0  |  提交时间:2019/12/19
Eliminating bacteria backbone of naked DNA enhanced hFIX expression and reduced inflammatory response in mice 期刊论文
BIOMEDICINE & PHARMACOTHERAPY, 2009, 卷号: 63, 期号: 2
作者:  Zhu, Huan-Zhang;  Chen, Hong-Yan;  Feng, Deng-Min;  Shen, Qi;  Xue, Jing-Lun
收藏  |  浏览/下载:5/0  |  提交时间:2019/12/19
A comparative study of hFIX expression mediated by rAAV8 and rAAV1 administrated intramuscularly 期刊论文
2007, 卷号: 9, 期号: 6, 页码: 593
作者:  Cao, Z[1];  Zheng, P;  Lin, Y
收藏  |  浏览/下载:1/0  |  提交时间:2019/12/06
Efficient expression of human factor IX cDNA in liver mediated by hydrodynamics-based plasmid administration 期刊论文
CHINESE SCIENCE BULLETIN, 2003, 卷号: 48, 期号: 8
作者:  He, CX;  Feng, DM;  Wu, WJ;  Ding, YF;  Chen, L
收藏  |  浏览/下载:2/0  |  提交时间:2019/12/27
Preparation of rAAV/hFIX by HSV/AAV hybrid helper virus and evaluation of its safety 期刊论文
CHINESE SCIENCE BULLETIN, 2003, 卷号: 48, 期号: 13
作者:  Chen, L;  Chen, HM;  Zou, BY;  Wu, ZJ;  Wu, XB
收藏  |  浏览/下载:4/0  |  提交时间:2019/12/27


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