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Editing Aberrant Splice Sites with Cas9 and Cas12a Efficiently Restores beta-Globin Expression in beta-Thalassemia 会议论文
22nd Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT), APR 29-MAY 02, 2019
作者:  Luk, Kevin;  Xu, Shuqian;  Yao, Qiuming;  Shen, Anne H.;  Zeng, Jing
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