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Delivery of Glucosylceramidase Beta Gene Using AAV9 Vector Therapy as a Treatment Strategy in Mouse Models of Gaucher Disease
Jiang, Nan; Du, Sichen; Ou, Huayuan; Cui, Renjie; Zhang, Meiqin; Li, Xiaorong; Ma, Jing; Zhang, Jin; Ma, Duan
刊名HUMAN GENE THERAPY
2019
卷号30期号:2
关键词Gaucher disease gene therapy AAV9 GD mouse model
ISSN号1043-0342
URL标识查看原文
语种英语
内容类型期刊论文
URI标识http://www.corc.org.cn/handle/1471x/3595053
专题复旦大学上海医学院
推荐引用方式
GB/T 7714
Jiang, Nan,Du, Sichen,Ou, Huayuan,et al. Delivery of Glucosylceramidase Beta Gene Using AAV9 Vector Therapy as a Treatment Strategy in Mouse Models of Gaucher Disease[J]. HUMAN GENE THERAPY,2019,30(2).
APA Jiang, Nan.,Du, Sichen.,Ou, Huayuan.,Cui, Renjie.,Zhang, Meiqin.,...&Ma, Duan.(2019).Delivery of Glucosylceramidase Beta Gene Using AAV9 Vector Therapy as a Treatment Strategy in Mouse Models of Gaucher Disease.HUMAN GENE THERAPY,30(2).
MLA Jiang, Nan,et al."Delivery of Glucosylceramidase Beta Gene Using AAV9 Vector Therapy as a Treatment Strategy in Mouse Models of Gaucher Disease".HUMAN GENE THERAPY 30.2(2019).
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